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Vliet, M. van der
( M. van der Vliet)
glucosidase enzyme acid α- glucosidase mouse expression cho cells gland lysosomal transgene activity production fraction precursor gsdii disease protein tissue fibroblast 76 kda 1-casein muscle storage medium glycogen sample natl acad cho cell medium enzyme replacement therapy figure mouse milk number reuser level fragment animal study m 6p receptor blot analysis 110 kda precursor gsdii ko mice fraction i enzyme patient therapy probe hopwood heart biochem genetic table receptor antibody sequence replacement a.j.j analysis fraction i promoter glucosidase activity copy number transgene expression anson epithelial cells model gsdii knockout mice mouse lines glycogenosis type ii concentration rabbit digestion result deficiency knockout placenta lysosomal glycogen storage source lysosomal storage diseases purification rabbit antibodies acids research preparation
2 Most Recent Publications
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Recombinant human acid α-glucosidase: High level production in mouse milk, biochemical characteristics, correction of enzyme deficiency in GSDII KO mice
(Article)
Bijvoet, A.G.A. Kroos, M.A. Pieper, F.R. Vliet, M. van der Boer, H.A. de Ploeg, A.T. van der Verbeet, M.P. Reuser, A.J.J. |
1998-10-01
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Recombinant human acid alpha-glucosidase: high level production in mouse milk, biochemical characteristics, correction of enzyme deficiency in GSDII KO mice
(Article)
Bijvoet, A.G. Kroos, M.A. Pieper, F.R. Vliet, M. van der Boer, H.A. Ploeg, A.T. van der Verbeet, M.P. Reuser, A.J.J. |
1998-01-01
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