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Verbeet, M.P.

( M.P. Verbeet)


glucosidase enzyme acid α- glucosidase mouse expression muscle disease lysosomal activity gsdii tissue knockout glycogen cho cells gland storage transgene protein production fraction precursor model heart knockout mice fibroblast figure 76 kda animal 1-casein reuser medium genetic glucosidase activity fragment sample study analysis patient natl acad sequence cho cell medium enzyme replacement therapy lysosomal glycogen storage deficiency a.j.j mouse milk table number level gsdii knockout mice wild-type therapy m 6p receptor blot analysis acids research glycogenosis type ii 110 kda precursor rabbit gsdii ko mice fraction i enzyme probe biochem glucosidase gene hopwood receptor antibody replacement anson transgene expression fraction i promoter copy number epithelial cells mouse lines concentration 6 weeks knockout mouse digestion placental acid result




3 Most Recent Publications

Recombinant human acid α-glucosidase: High level production in mouse milk, biochemical characteristics, correction of enzyme deficiency in GSDII KO mice (Article)
Bijvoet, A.G.A. Kroos, M.A. Pieper, F.R. Vliet, M. van der Boer, H.A. de Ploeg, A.T. van der Verbeet, M.P. Reuser, A.J.J.
1998-10-01
Generalized glycogen storage and cardiomegaly in a knockout mouse model of Pompe disease (Article)
Bijvoet, A.G. Ploeg, A.T. van der Reuser, A.J.J. Kamp, E.H. van de Kroos, M.A. Ding, J-H. Yang, B.Z. Visser, P. Bakker, C.E. Verbeet, M.P. Oostra, B.A.
1998-01-01
Recombinant human acid alpha-glucosidase: high level production in mouse milk, biochemical characteristics, correction of enzyme deficiency in GSDII KO mice (Article)
Bijvoet, A.G. Kroos, M.A. Pieper, F.R. Vliet, M. van der Boer, H.A. Ploeg, A.T. van der Verbeet, M.P. Reuser, A.J.J.
1998-01-01