doi.org/10.17650/2222-8721-2018-8-4-19-34, hdl.handle.net/1765/117305
Nervno-Myshechnye Bolezni
Department of Clinical Genetics

van der Ploeg, A., Kruijshaar, M., Toscano, A., Laforêt, P., Angelini, C., Lachmann, R., … Schoser, B. (2018). European consensus for starting and stopping enzyme replacement therapy in adult patients with Pompe disease: A 10-year experience. Nervno-Myshechnye Bolezni (Vol. 8, pp. 19–34). doi:10.17650/2222-8721-2018-8-4-19-34