doi.org/10.1182/bloodadvances.2019000811, hdl.handle.net/1765/121565
Blood Advances
Erasmus MC: University Medical Center Rotterdam

Drygalski, A.V. (Annette Von), Giermasz, A. (Adam), Castaman, G., Key, N.S. (Nigel S.), Lattimore, S. (Susan), Leebeek, F., … Pipe, S.W. (Steven W.). (2019). Etranacogene dezaparvovec (AMT-061 phase 2b): Normal/near normal FIX activity and bleed cessation in hemophilia B. Blood Advances, 3(21), 3241–3247. doi:10.1182/bloodadvances.2019000811