mitochondrial neurogastrointestinal encephalomyopathy, MNGIE, thymidine phosphorylase, metabolic disease, Hematopoietic stem cell gene therapy, ex vivo transduction, lentiviral vector
P.A.E. Sillevis Smitt (Peter) , N.P. van Til (Niek) , I.F.M. de Coo (René)
Erasmus University Rotterdam
The research in this thesis was financially supported by the European Commission’s 5th, 6th and 7th Framework Programs, CONSERT, CELL-PID, PERSIST , and by the Netherlands Health Research and Development Organization ZonMw, Join4energy, Ride4Kids, and the Sophia Foundation (SSW0645) and Stichting NeMo.
Department of Neurology

Yadak, R.M.A. (2017, December 19). Lentiviral Hematopoietic Stem Cell Gene Therapy for MNGIE. Erasmus University Rotterdam. Retrieved from

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