Additional Metadata
Keywords mitochondrial neurogastrointestinal encephalomyopathy, MNGIE, thymidine phosphorylase, metabolic disease, Hematopoietic stem cell gene therapy, ex vivo transduction, lentiviral vector
Promotor P.A.E. Sillevis Smitt (Peter) , N.P. van Til (Niek) , I.F.M. de Coo (René)
Publisher Erasmus University Rotterdam
Sponsor The research in this thesis was financially supported by the European Commission’s 5th, 6th and 7th Framework Programs, CONSERT, CELL-PID, PERSIST , and by the Netherlands Health Research and Development Organization ZonMw, Join4energy, Ride4Kids, and the Sophia Foundation (SSW0645) and Stichting NeMo.
ISBN 978-94-6182-857-6
Persistent URL
Yadak, R.M.A. (2017, December 19). Lentiviral Hematopoietic Stem Cell Gene Therapy for MNGIE. Erasmus University Rotterdam. Retrieved from